Gene Therapy

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Wooden blocks which say PHASE and a block at the end with the numbers 1/2. The last block is switching from 1 to 2. This represents a clinical trial moving through phases. Image credit: ©rabbitti – stock.adobe.com
First patient dosed in Phase 1/2 ASTRA study for Stargardt disease therapy SB-007 (SpliceBio)

March 13th 2025

SpliceBio continues to actively enroll patients in the ASTRA study and accompanying POLARIS trial

Figure. Slit-scanning in vivo confocal microscopy images of the corneal endothelium: A (left) demonstrates a healthy control cornea: Image of a normal corneal endothelium, showing a uniform hexagonal cell pattern with consistent cell density and no visible guttae or abnormalities (white solid arrowhead). B (right) shows FECD: Increased confluency of guttata, illustrating a more extensive presence of these structures. Images courtesy UCL/NIHR Moorfields Biomedical Research Centre.
Study links new gender and genetic factors to Fuchs Endothelial Corneal Dystrophy

March 13th 2025

Two illustrated DNA helices on a blue background. Image credit: ©rost9 – stock.adobe.com
EMA provides positive ATMP opinion for gene therapy products OCU410 and OCU410ST

March 4th 2025

An illustration of an eye's iris and pupil, suspended on a dark background which evokes the depth of outer space. Image credit: ©Enis – stock.adobe.com
Novel stem cell therapy restores corneal damage previously believed irreversible

March 4th 2025

Study demonstrates visual acuity improvements following gene therapy for AIPL1-associated inherited retinal dystrophies
Study demonstrates visual acuity improvements following gene therapy for AIPL1-associated inherited retinal dystrophies

February 25th 2025

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Latest CME Events & Activities

Navigating the Advances in the Treatment of Geographic Atrophy: Updates and Strategies for Managed Care

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CRU Eye Symposium

March 28-30, 2025

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The Neural Network: Exploring the Role of Neuromodulation in Dry Eye Disease Management

April 2025

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Surv.AI Says: Real-World Insights Into Patient Burden & Evolving Strategies in nAMD and DME (CME Credit)

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Community Practice Connections™: Optimizing Outcomes in Glaucoma Management - Applying Evidence to Practice with a Multitude of Treatment Options (CME Track)

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Community Practice Connections™: Mastering the New Treatment Paradigm in Geographic Atrophy – From Detection to Intervention (CME Track)

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Assessing the Evidence for Extending Treatment Intervals in nAMD and DME Management – Expert Insights into Innovative Approaches (CME Track)

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Assessing the Evidence for Extending Treatment Intervals in nAMD and DME Management – Expert Insights into Innovative Approaches (COPE Track)

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Uncovering Neurotrophic Keratitis: Exploring Hidden Manifestations and Key Patient Demographics (CME Track)

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Uncovering Neurotrophic Keratitis: Exploring Hidden Manifestations and Key Patient Demographics (COPE Track)

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Surv.AI Says: Real-World Insights into Patient Burden & Evolving Strategies in nAMD and DME (COPE Credit)

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Community Practice Connections™: Mastering the New Treatment Paradigm in Geographic Atrophy – From Detection to Intervention (COPE Track)

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Community Practice Connections™: Optimizing Outcomes in Glaucoma Management - Applying Evidence to Practice with a Multitude of Treatment Options (COPE Track)

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Reimagining Dry Eye Disease: Delineating the Role of Evaporation From Inflammation and Insights Into Optimizing Treatment (CME Track)

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Reimagining Dry Eye Disease: Delineating the Role of Evaporation From Inflammation and Insights Into Optimizing Treatment (COPE Track)

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19th Annual Controversies in Modern Eye Care

May 4, 2025

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(CME Track) Community Practice Connections™: Advancing the Optimal Diagnosis & Treatment of Thyroid Eye Disease

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(COPE Track) Community Practice Connections™: Advancing the Optimal Diagnosis & Treatment of Thyroid Eye Disease

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(CME) Community Practice Connections™: A Closer Look at Neurotrophic Keratitis—Ensuring Timely Diagnosis and Taking Early Action

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Outlining the New Standard in Geographic Atrophy: Optimizing Care Within the Modern Treatment Paradigm (COPE Track)

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Outlining the New Standard in Geographic Atrophy: Optimizing Care Within the Modern Treatment Paradigm (CME Track)

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Collaborative Care Symposium

May 30-31, 2025

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Community Practice Connections™: Novel Therapies for Neovascular Retinal Disease – Expert Analysis of New Key Data

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Latest Advances in X-Linked Retinitis Pigmentosa: Optimizing Diagnosis and Developments in Gene Therapy

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Cases & Conversations™: Real World Review of Treat and Extend Strategies for Neovascular Retinal Disease

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Community Practice Connections™: Innovations and Interdisciplinary Approaches in Glaucoma Management—Expanding the Treatment Arsenal (CME Track)

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Community Practice Connections™: Innovations and Interdisciplinary Approaches in Glaucoma Management—Expanding the Treatment Arsenal (COPE Track)

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Road Mapping the Treat-and-Extend Protocol in nAMD and DME – When Time Is Sight (CME Track)

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Road Mapping the Treat-and-Extend Protocol in nAMD and DME – When Time Is Sight (COPE Track)

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Community Practice Connections™: Navigating Complexities in Neurotrophic Keratitis — A Roadmap for Advanced Patient Care (CME Credit)

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